The Science
Behind the Breakthrough

Popcorn Platform

The Popcorn platform is a first-in-class modular therapeutic oncolytic adenovirus delivery system designed to produce single-domain functional antibodies against any chosen target within the tumor microenvironment, accelerating translation across tumor types.

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Brain Tumors: The #1 Cancer
Killer in Children

DMG is not just rare and aggressive — it occupies the brainstem, making surgical resection impossible and conventional drug delivery irrelevant.

Patients remain mentally aware while progressively losing vital functions: vision, swallowing, movement, breathing.

Radiotherapy, chemotherapy, targeted therapies, and adult immunotherapy have all failed. There is currently no effective treatment.

75–80%
DMG represents 75-80% of pediatric brainstem tumors
12 mo
Median survival after diagnosis
90%
Patients die within 2 years of onset
1
Effective treatments currently approved
POP02 Lead Program – Triple Action

How It Works

Scroll to see how POP02's three simultaneous mechanisms address the specific barriers that have made DMG untreatable.

Step 1 — Direct Attack

Viral Oncolysis

POP02 replicates exclusively within tumor cells, directly destroying cancer tissue while leaving healthy neural cells completely unharmed.

Intratumoral Delivery
Step 2 — Immune Activation

41BB Agonist

Localized immune co-stimulation activates CD4 and CD8 T cells precisely within the tumor microenvironment — avoiding systemic toxicity.

Laspidea et al. JCI Insight (2022)
Step 3 — Checkpoint Blockade

TIM3 Antagonist

Blocks immune suppression checkpoints, allowing the body's natural defenses to sustain the anti-tumor response long after initial treatment.

Ausejo-Mauleon et al. Cancer Cell (2023)
Result

Tumor Elimination

In the most aggressive preclinical DMG models, POP02 produced long-term survivors free of disease — an outcome not achieved by DNX2401, B7H3 CAR-T, or ONC201.

Best-in-class vs DNX2401, B7H3 CAR-T, ONC201
Scroll

POP02 is built on DNX2401 — an oncolytic adenovirus with established human safety and demonstrated anti-tumor activity in peer-reviewed Phase I trials.

Pre-clinical Validation
Martinez-Velez et al.
Nature Communications
2019

First demonstration of DNX2401 efficacy in DMG preclinical models

Clinical Phase I
Gallego Perez-Larraya et al.
New England Journal of Medicine
2022

Phase I clinical trial proving safety and preliminary efficacy in humans

Why POP02 Can Succeed
Where Others Have Failed

Validated Backbone

Built on DNX2401, the only oncolytic adenovirus with proven clinical activity in high-grade gliomas — including compassionate-use data in pediatric DMG.

Modular Architecture

Single-domain antibody (sdAb) payload is interchangeable — the same viral chassis can be re-armed against different immune targets with minimal re-engineering.

BBB Penetration

Direct intratumoral delivery bypasses the blood–brain barrier — the major pharmacological obstacle that has defeated all systemic therapies in DMG.

Pediatric Safety Profile

Adenovirus vectors carry an established pediatric safety record. No DNA integration risk. POP02 replication is restricted to H3K27M-mutant tumor cells.

Regulatory Pathway

Orphan Drug Designation eligibility (FDA + EMA) provides 10-year market exclusivity, priority review, and fee waivers. Breakthrough Therapy application planned post-Phase I proof-of-concept.

Published in the World's Top Medical Journals

Scroll to browse publications

01 / 12
01
2019
Nature Communications
Pre-clinical validation of DNX2401 in DMG models — foundational evidence for the backbone platform
Martinez-Velez et al.
02
2019
Acta Neuropathologica Communications
Delta-24-RGD combined with radiotherapy — potent antitumor effect in DIPG and pediatric high-grade glioma models
Martinez-Velez et al.
03
2021
Clinical Cancer Research
Delta-24-RGD increases survival and drives proinflammatory immune remodeling in AT/RT and CNS-PNET models
Garcia-Moure et al.
04
2022
New England Journal of Medicine
Phase I Clinical Trial — safety and efficacy of DNX2401 in humans
Gallego Perez-Larraya et al.
05
2022
JCI Insight
41BBL oncolytic virus — efficacy and toxicology validation in preclinical models
Laspidea et al.
06
2022
Molecular Cancer Therapeutics
4-1BBL armed oncolytic adenovirus drives antitumor effect and immune memory in a pediatric osteosarcoma model
Martinez-Velez et al.
07
2022
Frontiers in Immunology
Immunovirotherapy for pediatric solid tumors — a promising treatment becoming clinical reality
de la Nava et al.
08
2023
Cancer Cell
TIM3 role in DMG — long-term survivors free of disease in preclinical models
Ausejo-Mauleon et al.
09
2023
Revue Neurologique
Oncolytic virotherapy for the treatment of pediatric brainstem gliomas — a clinical perspective
Pérez-Larraya et al.
10
2024
JCI Insight
Locoregional radiotherapy combined with a TIM-3 aptamer improves survival in diffuse midline glioma models
Ausejo-Mauleon et al.
11
2024
Clinical & Translational Medicine
The rise of TIM-3 — a promising immune target in diffuse midline gliomas
Ausejo-Mauleon et al.
12
2024
Neuro-Oncology
Delta-24-RGD in combination with ONC201 — potent antitumor response in pediatric high-grade and diffuse midline glioma models
de la Nava et al.

See Our Pipeline

POP02 is our lead program targeting pediatric DMG, with platform expansion into adult GBM already in preclinical development.

View Pipeline Investor Information